Junk DNA in birds could be key to safe and effective gene therapy
Retrotransposons found in the genomes of the white-throated sparrow and zebra finch have been shown to safely introduce transgenes into ...
Tag: therapy
Promising target for CAR T cell therapy leads to powerful anti-tumor responses against cutaneous and rare melanomas
A co-culture image showing clusters of CAR T cells attacking tumor cells (in green). Credit: Puig-Saus Laboratory. Scientists at UCLA ...
New gene therapy shows promise for motor neuron disease and frontotemporal dementia
Credit: Neuron (2024). DOI: 10.1016/j.neuron.2024.01.022 Macquarie University neuroscientists have developed a single-dose genetic drug proven to halt the progression of ...
Gene therapy to help chronic heart failure
The leading cause of death in the United States, heart failure can be treated with gene therapy. A new study ...
New strategy for safer CAR T cell therapy in lymphomas
Graphical summary. Credit: Cell Reports Medicine (2024). DOI: 10.1016/j.xcrm.2024.101421 In the treatment of aggressive lymphomas and blood cancer (leukemia), chimeric ...
New cell therapy shows promise in patients with acute respiratory distress syndrome
Credit: Pixabay/CC0 Public domain Promising trial results indicate that a new type of cell therapy could improve the prognosis of ...
Combination drug therapy shows promise for treatment-resistant cancer
Christine Pratilas, MD, in the lab. Credit: Frederick W. Dubs, Johns Hopkins Pathology Photography & Graphics A combination of two ...
New AI model designs proteins to deliver gene therapy
ProteinVAE architecture. Encoder: The pre-trained language model (e.g., ProtBert) converts the input one-hot encoded sequences to amino acid-level representation H. ...
Real-time magnetic resonance imaging during convective gene therapy in the brain
Credit: CC0 Public domain Real-time magnetic resonance imaging (MRI) during gene therapy in the nervous system has a fundamental impact ...
Gene therapy restores hearing in children with hereditary deafness
Credit: Pixabay/CC0 Public domain A new study co-led by researchers at Mass Eye and Ear, part of Mass General Brigham, ...
